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Search results for "rare diseases"

Viewing 1 - 20 of 416 results by relevance
Consensus Study Report

Rare Diseases and Orphan Products: Accelerating Research and Development  (2010)

Proceedings

Breakthrough Business Models: Drug Development for Rare and Neglected Diseases and Individualized Therapies: Workshop Summary  (2009)

Proceedings

Implementing and Evaluating Genomic Screening Programs in Health Care Systems: Proceedings of a Workshop  (2018)

Proceedings

Refining Processes for the Co-Development of Genome-Based Therapeutics and Companion Diagnostic Tests: Workshop Summary  (2014)

Consensus Study Report

Managing the NIH Bethesda Campus Capital Assets for Success in a Highly Competitive Global Biomedical Research Environment  (2019)

Forum on Drug Discovery, Development, and Translation: 2010 Annual Report  (2011)

Proceedings

Relevance of Health Literacy to Precision Medicine: Proceedings of a Workshop  (2016)

Proceedings

Diffusion and Use of Genomic Innovations in Health and Medicine: Workshop Summary  (2008)

Consensus Study Report

Adverse Effects of Vaccines: Evidence and Causality  (2012)

Proceedings

Drug Repurposing and Repositioning: Workshop Summary  (2014)

Roundtable on Translating Genomic-Based Research for Health: 2012 Annual Report  (2013)

Proceedings

Toward Sequencing and Mapping of RNA Modifications: Proceedings of a Workshop–in Brief  (2023)

Proceedings

Third International Summit on Human Genome Editing: Expanding Capabilities, Participation, and Access: Proceedings of a Workshop—in Brief  (2023)

Proceedings

The Food and Drug Administration's Accelerated Approval Process for New Pharmaceuticals: Proceedings of a Workshop—in Brief  (2023)

Consensus Study Report

NIH Extramural Center Programs: Criteria for Initiation and Evaluation  (2004)

Roundtable on Translating Genomic-Based Research for Health: 2013 Annual Report  (2014)

Roundtable on Translating Genomic-Based Research for Health: 2011 Annual Report  (2012)

Proceedings

Enabling Precision Medicine: The Role of Genetics in Clinical Drug Development: Proceedings of a Workshop  (2017)

Proceedings

Methodologies for Evaluating and Grading Evidence: Considerations for Public Health Emergency Preparedness and Response: Proceedings of a Workshop—in Brief  (2019)