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Search results for "gene therapies"

Viewing 1 - 20 of 132 results by relevance
Proceedings

Exploring Novel Clinical Trial Designs for Gene-Based Therapies: Proceedings of a Workshop  (2020)

Proceedings

Advancing Gene-Targeted Therapies for Central Nervous System Disorders: Proceedings of a Workshop  (2019)

Proceedings

Applying Systems Thinking to Regenerative Medicine: Proceedings of a Workshop  (2021)

Transforming Human Health: Celebrating 50 Years of Discovery and Progress  (2022)

Proceedings

Exploring the State of the Science in the Field of Regenerative Medicine: Challenges of and Opportunities for Cellular Therapies: Proceedings of a Workshop  (2017)

Proceedings

Emerging Technologies and Innovation in Manufacturing Regenerative Medicine Therapies: Proceedings of a Workshop–in Brief  (2024)

Forum on Regenerative Medicine: 2018 and 2019 Program Activities  (2020)

Proceedings

Third International Summit on Human Genome Editing: Expanding Capabilities, Participation, and Access: Proceedings of a Workshop—in Brief  (2023)

Forum on Regenerative Medicine: 2020 Annual Report  (2021)

Proceedings

Navigating the Manufacturing Process and Ensuring the Quality of Regenerative Medicine Therapies: Proceedings of a Workshop  (2017)

Forum on Neuroscience and Nervous System Disorders: 2017 Annual Report  (2018)

Consensus Study Report

Oversight and Review of Clinical Gene Transfer Protocols: Assessing the Role of the Recombinant DNA Advisory Committee  (2014)

Consensus Study Report

Mitochondrial Replacement Techniques: Ethical, Social, and Policy Considerations  (2016)

Forum on Regenerative Medicine: 2023 Annual Report  (2024)

Forum on Neuroscience and Nervous System Disorders: 2016 Annual Report  (2017)

Proceedings

Second International Summit on Human Genome Editing: Continuing the Global Discussion: Proceedings of a Workshop–in Brief  (2019)

Proceedings

Exploring Sources of Variability Related to the Clinical Translation of Regenerative Engineering Products: Proceedings of a Workshop  (2019)

Proceedings

Innovation in Drug Research and Development for Prevalent Chronic Diseases: Proceedings of a Workshop  (2021)

Proceedings

Successes and Challenges in Biomanufacturing: Proceedings of a Workshop–in Brief  (2023)

Proceedings

Continuous Manufacturing for the Modernization of Pharmaceutical Production: Proceedings of a Workshop  (2019)